A little boy was diagnosed with a life-limiting, muscular condition after his parents realised he was unable to jump. Kairo Barranco, seven, was diagnosed with Duchenne muscular dystrophy (DMD) – a ...

Cancer cachexia is a multifactorial syndrome marked by a severe loss of body weight due primarily to the wasting of skeletal muscle and adipose tissue. This syndrome is often accompanied by systemic ...

The EMA has backed broader pediatric use of Agamree and Crysvita, lowering age thresholds for rare genetic diseases affecting muscle and bone development.

Late-stage trial data for Roche’s drug against muscle-wasting Elevidys showed positive results after two years of treatment for male patients aged 4 or older with Duchenne muscular dystrophy. The data ...

Oct 31 (Reuters) - Sarepta Therapeutics shares (SRPT.O), opens new tab fell nearly 44% on Tuesday, after its gene therapy for a progressive muscle-wasting disorder failed to meet the main goal in a ...

Loss of muscle mass, also called muscle wasting or atrophy, can happen gradually as part of getting older or more suddenly due to underlying medical conditions. Other factors can contribute, like ...

DECEMBER 3, 2025—(BRONX, NY)—Two related studies published today in Nature Metabolism show that a specialized intracellular recycling mechanism—chaperone-mediated autophagy (CMA)—is essential for ...

March 28 (Reuters) - PTC Therapeutics (PTCT.O), opens new tab said on Friday its inherited progressive muscle-wasting disorder drug will no longer be available for sale in the EU as the European ...

University of Pittsburgh School of Medicine researchers carrying out a small pilot clinical trial demonstrating that a drug-free, minimally invasive intervention targets the root cause of progressive ...