Saffie Sandford was born with Leber's Congenital Amaurosis and "missed out on a lot" due to difficulties seeing in any ...

Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical ...

You might like the sound of this news. In a landmark move, the Food and Drug Administration on Thursday approved the first ...

Travis Smith was a very serious baby. Born completely unable to hear, his mother, Sierra, struggled to see his personality ...

The treatment, the first of its kind, was approved by the Food and Drug Administration on Thursday. “Our baby was born deaf, ...

As cell and gene therapy leaders gathered in Maryland to discuss accelerating clinical trials in children, one “cutting edge” ...

Three Philadelphia scientists won a $3 million Breakthrough Prize for developing the first FDA-approved gene therapy for a genetic disease, prize sponsors announced Saturday. Their work created a ...

Aradigm Health CEO Will Shrank discusses the shift in value-based care models for cell and gene therapies. While advances in ...

While advances in cell & gene therapy continue to show promise for creating new treatments, this sector of the industry still ...

A gene found in salamanders could one day help humans regrow lost limbs, a breakthrough that sounds like science fiction but ...